UCSF Broad Stem Cell
@UCSFstemcell
Discovering the inner workings of stem cells, engineering treatments using genome editing tools, and healing patients by developing life-saving therapies.
What if we could treat genetic disease before birth? Researchers found that injecting medicine into amniotic fluid may prevent spinal muscular atrophy, protecting nerve cells before damage begins. tiny.ucsf.edu/8GmmGX
Sarah will now be presenting virtually on Thursday 4/24. Hope to see you there! humangenetics.ucsf.edu/mapping-human-…
It's #WorldBrainDay! The brain controls everything that makes life possible. Scientific research provides the tools and knowledge needed to protect, restore, and enhance brain health for all. Are you a #neurowiz? Take this short quiz to find out: vist.ly/3yr5z
The University of California is innovating in artificial intelligence, healthcare, national defense, energy independence, and cybersecurity. Our @UofCalifornia community is problem-solving today for tomorrow’s challenges and driving the economy across the state and nation.…
Why Is Discovery Research So Important? @UCSFstemcell member Grae Davis unpacks how big breakthroughs happen and why public understanding of science matters: magazine.ucsf.edu/why-discovery-…

CIRM’s DISC5 funding program supports innovative, exploratory research in #StemCell biology and #RegenerativeMedicine, focusing on interdisciplinary pairs of investigators tackling key knowledge gaps. Learn more at cirm.ca.gov/disc5
It's finally out! Thankful for my mentor @Kriegsteinlab and all collaborators🙏 nature.com/articles/s4146…
Check out our new paper led by the brilliant @homamajd! Grateful to our fantastic collaborators for their insights and teamwork.
Our ENS is vital to gut-brain health. When it breaks down, so does health. Treatments? Almost none. Access to functional human enteric neurons at scale powers research, disease modeling and therapeutic discovery. Grateful to everyone who made this possible.nature.com/articles/s4158…
Dear colleagues and friends, please join to Celebrate the life of Atul Butte on Saturday at 10am. Co-hosted by @ucsf, @Stanford @Harvard
With deep sadness, we share the passing of Dr. Atul Butte—a visionary leader, scientist, and mentor. His groundbreaking work and boundless compassion transformed medicine and inspired so many. His legacy will continue to shape the University of California and beyond.
Excited for Huaigeng Xu’s talk “Engineered Universal iPSC-derived Dendritic Cells Dressed with Tumor-MHC-Peptide Complexes as a Cancer Vaccine,” at ISSCR 2025 session on AI and Cancer Evolution Friday 8:30 am. #isscr2025 @ucsfurology, @ucsf @ucsfcancer @ucsfstemcell @CIRMnews
LIVE NOW: FDA's Cell and Gene Therapy Roundtable Captions available here: bit.ly/4dQaNaz
live today! proud to have presented and contributed to the curriculum in the open-access @ISSCR course, Stem Cell Medicine: From Research to Patient Care, jointly with harvard med! This resource is a major milestone for the field at such a pivotal time. invt.io/1txb7nt8018
Geoffrey Manley, MD, PhD, chief of neurosurgery at @zsfgcare, worked with an international team to develop a new, more precise framework for diagnosing traumatic brain injuries. Learn about how the new criteria could reshape treatment and follow-up care ⬇️ l8r.it/KQPs
Join us for Getting to Patients on Thurs, 5/29! Dr. Matthay will share “Allogeneic Bone Marrow-Derived Mesenchymal Stromal Cells for ARDS: Pre-Clinical and Clinical Data” with patient perspective and discussion moderated by Dr. Julia Brown tiny.ucsf.edu/StromalCellsAR…

In the latest Science in Seconds, Bruce Conklin and Bria Macklin describe how they use cells collected from patients with CMT to explore how #GeneEditing can be used as a therapeutic tool to treat the disease. @TheConklinLab @brialmacklin bit.ly/3GTFcsc
The rapid advancement of CRISPR-Cas gene editing is transforming medicine, offering precise treatments for genetic disorders. UNCOVERseq, a new method, improves detection of off-target edits, enhancing safety and effectiveness. Read more: bit.ly/UNCOVERseq
Just released our pre-print on bioRxiv for UNCOVERseq, an improved off-target discovery platform for Cas9 and base editors! Great collaboration with the awesome team at IDT @idtdna biorxiv.org/content/10.110…
Hear how gene therapies can address serious genetic diseases before birth. @MacKenzieTippi will deliver a George Stamatoyannopoulos Memorial Lecture at the @ASGCT Annual Meeting on May 15. #ASGCT2025 #GeneTherapy #PrenatalResearch #raredisease

Meet our #ASGCT2025 keynote speakers: Drs. Drew Weissman, Tippi MacKenzie, Mike McCune, & Kiran Musunuru! Their talks will shape the future of #CGT-don’t miss out on their transformative sessions. View the full program here: bit.ly/44tWXIq
Fantastic opportunity for undergradute students interested in 🧠#BrainHealth #hydrocephalus #research #sciencepolicy w/ the outstanding @HydroAssoc . Patients, families, funders and researchers to #curehydrocephalus 🩺👩🏼⚕️💰🔬@UCSFNeo @UCSFPediatrics @NeoTECaN
Applications are now open! We are now accepting applications for the Ralph Kistler Research Internship. The internship is for undergraduate college students interested in the sciences, public health, and non-profit operations. Learn more➡️hydroassoc.org/ralph-kistler-…