Muscular Dystrophy News Today

Del-zota was granted FDA breakthrough therapy designation for treating DMD, and its developer is on track to seek its regulatory approval. buff.ly/QV0Ncjl #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

A public workshop that columnist Shalom Lim and his girlfriend, Amanda, organized aimed to foster connection among people with disabilities. musculardystrophynews.com/columns/how-ar… #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

The FDA asked Sarepta to pause all U.S. shipments of the DMD gene therapy Elevidys, and the company has agreed after initially refusing. buff.ly/5MDLFsp #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

Columnist Patrick Moeschen emphasizes the importance of making advance directives and shares some tips for how to get started. buff.ly/2HMGL8w #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

While looking at a hotel mirror, columnist Betty Vertin reflects on the past 15 years of raising three sons with DMD. buff.ly/h2GpmAM #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

The first patient has been dosed in a clinical trial testing Sardocor's one-time gene therapy for cardiomyopathy associated with Duchenne MD. buff.ly/fO3oaPI #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

Dealing with pain has become increasingly challenging for columnist Robin Stemple, who struggles to find relief from the hurt. buff.ly/I0DeUAF #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

Capricor plans to resubmit its application for the approval of deramiocel for DMD after the FDA declined to accept the original proposal. musculardystrophynews.com/news/capricor-… #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

Columnist Betty Vertin embraces July's slower pace, a much-needed respite from caregiving demands for her family of nine. buff.ly/tGOb6Si #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

A research team collected pain and prescription data from the medical records of 1,282 people with different types of muscular dystrophy. musculardystrophynews.com/news/third-mus… #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

Columnist Shalom Lim is energized by a recent program for youth leaders in Singapore that matched them with people from the MD community. buff.ly/Lm4ZPA9 #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

Households incur substantial costs to accommodate Duchenne muscular dystrophy (DMD) patients, according to a survey of U.S. caregivers. buff.ly/z6GgJOQ #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

We all have different tolerance levels for how much risk we'll accept when we do a risk vs. reward analysis, says columnist Patrick Moeschen. musculardystrophynews.com/columns/what-r… #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

After a busy year, columnist Betty Vertin is grateful that her three sons with DMD always have one another for socializing. buff.ly/kdJK7Fc #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

Researchers identified a unique protein signature in the blood of BMD and LGMD patients that may reflect disease progression. buff.ly/zykTrLv #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

Summer can be rough for folks with muscular dystrophy, columnist Patrick Moeschen writes, but it can also bring adventures in appreciation. buff.ly/GMpRhQi #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

Ifetroban improved heart function and reduced cardiac damage biomarkers in people with DMD in a Phase 2 clinical trial. buff.ly/7ATFO9J #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

Columnist Betty Vertin is grateful to have the help of a hired caregiver, but it's also been a difficult adjustment, she says. buff.ly/shtjxpS #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

The FDA has granted rare pediatric disease designation to PBGENE-DMD, an experimental gene-editing therapy for Duchenne muscular dystrophy. buff.ly/tmCsugX #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

A recent dream leaves columnist Robin Stemple questioning how his disability progression due to FSHD affects his family and friends. buff.ly/MYSC5iN #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD